CheckRare
@checkrare
Leading publisher and learning platform focused on rare diseases.
Rare Diseases Are Our Focus, Expertise, and Passion.
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http://www.checkrare.com 22-12-2016 18:39:42
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Stephen Russell, MD, Carver College of Medicine, discusses long-term data on Luxturna (voretigene neparvovec-rzyl) for retinal dystrophy treatment. #CheckRare #RareDisease #RetinalDystrophy checkrare.com/gene-therapy-l…
Dana Rizk, MD, Professor of Medicine at UAB Medicine, discusses the U.S. Food and Drug Administration (FDA) accelerated approval of Fabhalta (iptacopan) for the reduction of proteinuria in adults with IgA nephropathy. #IgAN #CheckRare #RareDisease checkrare.com/accelerated-ap…
Corey Cutler, MD, Director of Adult Stem Cell Transplantation Program at Dana-Farber and a Professor of Medicine at Harvard Medical School, discusses the approval of Niktimvo (axatilimab) for the treatment of chronic graft versus host disease. #GVHD #CheckRare checkrare.com/fda-approves-t…
Ponni Subbiah, MD, Senior Vice President of Acadia Pharmaceuticals, Global Head of Medical Affairs and Chief Medical Officer, discusses long-term data from clinical trial extension of trofinetide in patients with Rett syndrome. #CheckRare #RareDisease #RettSyndrome checkrare.com/long-term-data…
Prem Subramanian, MD, PhD, Professor of Ophthalmology at CU School of Medicine, discusses long-term data testing teprotumumab in patients with thyroid eye disease. #TED #CheckRare #RareDisease checkrare.com/long-term-data…