We are so excited to kick off #WorldOrphanUSA 's speaker announcements for 2025 by welcoming Pamela Gavin, CEO, NORD!

Register as a group and save up to 50% on your 2025 tickets today: tinyurl.com/ye2x5dak

🗓️ April 22-24, 2025
📍 Boston Convention & Exhibition Center

🗞️ Hot off the Press: #WorldOrphanUSA !
Our 2024 press roundup is here ➡️ tinyurl.com/2bwpej54

Plus, join us back at the Boston Convention & Exhibition Center April 22-24 for our 2025 edition! ⭐️
Register as a group & save up to 50% on tickets here ➡️ tinyurl.com/ye2x5dak

#ICYMI our CEO, Aki Ko, attended the 2024 World Orphan Drug Congress USA. He shared a presentation focused on the promise of local #CellTherapy processing. It was great to hear from industry peers about updates in #DrugDevelopment across #RareDiseases . World Orphan Drug Congress USA

WODC 2024: WRAP-UP POST (PART 1)

AHF is thankful to the organizers of the 2024 World Orphan Drug Congress USA for the opportunity to participate and contribute to the dialogue to enhance policy, access and innovation in the field of Rare Diseases (Gina McHugh (Saure), +

WODC 2024: WRAP-UP POST (PART 2)

AHF is pleased to share the highlights of the Policy Panel '360 view: How do we improve access while we continue to promote innovation.'

Highlights:

- Many countries around the world have been adjusting their regulatory frameworks to raise +

We had an incredible time at the World Orphan Drug Congress USA 2024! Our team was honored to contribute to the discussions around accelerating rare disease treatments.

We're grateful to have played a part in the conversation around #orphandrugs and #raredisease treatments.
#WODC24 #WorldOrphanUSA

Our team was inspired by the unified focus on patient-centric approaches at the World Orphan Drug Congress USA last week. 💡

Discover our key takeaways over on our blog. 👇

eu1.hubs.ly/H08YbJ70

#ClinicalTrials #PrecisionMedicine

YHEC staff were delighted to be at World Orphan Drug Congress USA last week. Here is what Stuart Mealing had to say about his time there.
If you'd like to get in touch, email us at [email protected]
#WorldOrphan DrugCongress #WorldOrphan #WODC #RareDiseases #OrphanDrugs

#FECOERSomosTodos Nuestro director Diego Gil, participó en el World Orphan Drug Congress, en Boston, Estados Unidos. Se abordaron temas como
✅gestión de datos,
✅ mecanismos innovadores para garantizar el acceso,
✅ equidad en el acceso a los ensayos clínicos, entre otros. 🧵

#WorldOrphanUSA : Clinical experts and advocates call for improving children’s access to essential health care by streamlining the Medicaid provider screening & enrollment process for out-of-state providers

Read more: brnw.ch/21wJdXb

#RDAatWODC World Orphan Drug Congress USA NORD

New data presented at this year's World Orphan Drug Congress USA (w/@WayneState) shows that #ATH434 behaves like a chaperone to redistribute iron within the body.

#wodc2024 #friedreichsataxia
#neurodegenerativedisease
bit.ly/4a2gfUm

We had an incredible time spreading awareness and knowledge of nano-rare last week at World Orphan Drug Congress USA 2024! Thank you to all who stopped by our n-Lorem info booth and attended our presentations. Until next year!

#WorldOrphanUSA : After a 25-year journey advancing basic, translational & clinical science, the Friedreich ataxia community saw a drug approved by the U.S. FDA last year to slow down the course of the disease. Read more: rarediseaseadvisor.com/reports/after-…

#RDAatWODC FA Research Alliance

#WorldOrphanUSA : 'These kids are not disposable.' - Patricia Welton founder and CEO of Beyond the Diagnosis.

World Orphan Drug Congress USA #RDAatWODC #OrphanDrugUSA #RareDisease

Our VP of Patient Advocacy, Cynthia Cassandro attended World Orphan Drug Congress USA’s #WorldOrphanUSA conference. Cynthia joined leaders on the panel: Challenges of Diagnosing & Treating Rare Diseases in Adult Patients. This was a great opportunity to share our experience in the #ALSP community.

We were honored to be part of World Orphan Drug Congress USA and join conversations driving real change for the #raredisease community 🙌When we come together, we make strides towards a brighter future for those affected by rare diseases. #WorldOrphanUSA #orphandrugs

Thank you to our attendees for making #WorldOrphanUSA a massive success — we could not have done it without you! ❤️‍🩹

Save the date! 🗓️ We'll be returning to Boston April 22-24, 2025. Stay tuned for more content from us in the meantime, and we hope to see you next year!

#WorldOrphanUSA : Heidi Ross, VP of policy and regulatory affairs at the National Organization for Rare Disorders (NORD), speaking at World Orphan Drug Congress USA.

#RDAatWODC #OrphanDrugUSA

#WorldOrphanUSA : Ron Bartek, President and Co-founder of FA Research Alliance, shares insights during a session focused on policies and strategies for improving #OrphanDrug accessibility.

World Orphan Drug Congress USA #RDAatWODC #GeneticTesting

#WorldOrphanUSA RDI World Orphan Drug Congress USA #RDAatWODC #OrphanDrugUSA